About the Lab
The main focus of the laboratory is the development of stem cell and gene therapy-based therapeutic approaches for metabolic and neurologic disorders, and the understanding of the mechanism of action for hematopoietic stem cell-mediated tissue repair.
Meet the PI

Dr. Cherqui is a professor at the University of California San Diego, Department of Pediatrics. She received her Ph.D in 2002 at Necker hospital (Paris, France); her research project focused on the molecular characterization of cystinosis, a metabolic hereditary disease, as well as the generation of mouse models. She then specialized in stem cells and gene therapy during her post-doctoral internship at The Scripps Research Institute where she was appointed Assistant Professor in 2009. In 2012, Dr. Cherqui joined the University of California, San Diego, Department of Pediatrics, Division of Genetics, became an Associate Professor in 2016, and Professor in 2022.